MPS VII - Disease Monitoring Program
This DMP will follow the disease in all enrolled individuals with MPS VII, regardless if they are receiving or not receiving Mepsevii. The DMP will observe how your disease changes over time by using several tests and questionnaires, which will be discussed later in this form. For those individualss who are receiving Mepsevii, this DMP will assess long-term effectiveness and safety of Mepsevii.
- All genders
- All Ages
- Volunteers with special conditions
- In Person
Who can participate?
Gender: All genders
Age: All Ages
Volunteers: Volunteers with special conditions
Location: In Person
Will I be paid for my time?